Methods for the Treatment of Trinucleotide Repeat Expansion Disorders Associated with FAN1 activity via Targeting of FAN1 Splice Site Inhibitory Sequences

Invention type: Technology / Case number: #24829
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Researchers

Christopher Ng / David Housman

Departments: David H Koch Institute for Integrative Cancer Res, Department of Biology
Technology Areas: Biotechnology: DNA & RNA Editing / Drug Discovery and Research Tools: Genomics & Proteomics / Therapeutics: Nucleic Acids
Impact Areas: Healthy Living

  • compositions and methods for treating fan1 associated trinucleotide repeat expansion disorders
    United States of America | Pending
  • compositions and methods for treating fan1 associated trinucleotide repeat expansion disorders
    Patent Cooperation Treaty | Pending

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