Methods for the Treatment of Trinucleotide Repeat Expansion Disorders Associated with FAN1 activity via Targeting of FAN1 Splice Site Inhibitory Sequences

Invention type: Technology / Case number: #24829
License tlo.mit.edu/contact-us

Researchers

Christopher Ng / David Housman

Departments: David H Koch Institute for Integrative Cancer Res, Department of Biology
Technology Areas: Biotechnology: DNA & RNA Editing / Drug Discovery and Research Tools: Genomics & Proteomics / Therapeutics: Nucleic Acids
Impact Areas: Healthy Living

  • compositions and methods for treating fan1 associated trinucleotide repeat expansion disorders¿
    United States of America | Pending

License this technology

Interested in this technology? Connect with our experienced licensing team to initiate the process.

Contact Us

Sign up for technology updates

Sign up now to receive the latest updates on cutting-edge technologies and innovations.

Sign Up

More Technologies

Multisensory Gamma Stimulation Promotes Glymphatic Clearance of Amyloid

#25696PH
Li-Huei Tsai / Edward Boyden / Ping-Chieh Pao / Cheng-Yi Yang / Mitchell Murdock
Biotechnology / Drug Discovery and Research Tools

Tuning Chloroplast Transgene Expression from Synthetic Operon

#25494
Christopher Voigt / Qiguo Yu
Agriculture & Food / Biotechnology / Therapeutics

A Multi-Pathway Reporter System that Interrogates Repair of DNA Double-Strand Breaks with Applications for Diagnosis and Therapeutic Treatment of Cancer and Neurodegenerative Diseases

#25444
Alex Kruswick / Michael Yaffe
Biotechnology / Diagnostics / Drug Discovery and Research Tools